Crushed deferasirox film-coated tablets in pediatric patients with transfusional hemosiderosis: Results from a single-arm, interventional phase 4 study (MIMAS)

TY - JOUR

T1 - Crushed deferasirox film-coated tablets in pediatric patients with transfusional hemosiderosis

T2 - Results from a single-arm, interventional phase 4 study (MIMAS)

AU - Wali, Yasser

AU - Hassan, Tamer

AU - Charoenkwan, Pimlak

AU - Trompeter, Sara

AU - Tartaglione, Immacolata

AU - Origa, Raffaella

AU - Gamberini, Maria Rita

AU - Viprakasit, Vip

AU - Izquierdo, Miguel

AU - Opio, Socrates

AU - Roy, Tania

AU - Taher, Ali

N1 - Funding Information: received research grants and honoraria from Takeda, Novo Nordisk, Pfizer, and Novartis. Shared in advisory boards for Takeda, Pfizer, and Novartis. reported consultancy for bluebird bio and honoraria from Celgene and Novartis; reported speakers' bureau fees from Novartis and membership of the advisory committee for bluebird bio and Novartis; are employees of Novartis; provided consultancy and received research funding from Novartis Pharmaceuticals, Bristol‐Myers Squibb, Imara, Vifor, IONIS Pharmaceuticals and provided consultancy to Agios. declared no conflicts of interest. Wali Y Tartaglione I Origa R Miguel I, Socrates O, and Tania R Taher A Hassan T, Charoenkwan P, Trompeter S, Gamberini MR, and Viprakasit V

PY - 2022/8

Y1 - 2022/8

KW - Benzoates/therapeutic use

KW - Child

KW - Deferasirox

KW - Hemosiderosis/etiology

KW - Humans

KW - Iron Chelating Agents/therapeutic use

KW - Iron Overload

KW - Tablets

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UR - https://www.mendeley.com/catalogue/5bd127d8-6c60-3553-9f6a-64fe16484b1c/

U2 - 10.1002/ajh.26598

DO - 10.1002/ajh.26598

M3 - Letter

C2 - 35570412

AN - SCOPUS:85130986558

SN - 0361-8609

VL - 97

SP - E292-E295

JO - American Journal of Hematology

JF - American Journal of Hematology

IS - 8

ER -